天使综合征药物研究进展汇总
clinicaltrials
- Phase 3 Efficacy and Safety Study of GTX-102 in Pediatric Subjects With AS
- Long-term Extension of GTX-102 in Angelman Syndrome
- Structural-functional Connectome in Drug-resistant Epilepsies and Neurodevelopmental Syndromes With Epilepsy
- Study of the Prevalence of Autistic Traits in Angelman Syndrome
- Natural History Study for Patients With Angelman Syndrome
- Promoting Prosocial Behavior in Syndromic Intellectual and Developmental Disabilities
- Angelman Natural History Study - FAST Spain
- IDMet (RaDiCo Cohort) (RaDiCo-IDMet)
- Development of a Newborn Screening Assay for Angelman Syndrome and Prader-Willi Syndrome
- Angelman Syndrome Video Assessment (ASVA) Source Material Study
- Study to Investigate the Pharmacokinetics and Safety and to Provide Proof of Mechanism of Alogabat in Children and Adolescents Aged 5-17 Years With Angelman Syndrome (AS) With Deletion Genotype.
- Study to Investigate the Pharmacokinetics and Safety and to Provide Proof of Mechanism of Alogabat in Children and Adolescents Aged 5-17 Years With Angelman Syndrome (AS) With Deletion Genotype
- The Global Angelman Syndrome Registry
- HALOS: A Safety, Tolerability, Pharmacokinetics and Pharmacodynamics Study of Multiple Ascending Doses of ION582 in Participants With Angelman Syndrome
- Angelman Syndrome Natural History Study-FAST UK
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